john24+FollowGene Therapy Lets Deaf Teens Hear!Imagine hearing for the first time at 24! A new study just proved gene therapy can restore hearing not just in kids, but also in teens and adults born deaf due to a rare gene mutation. Patients went from total silence to chatting at normal volumes—some even heard rain for the first time. The best part? No major side effects. This could be a total game-changer for thousands who thought hearing was impossible! #Health #BodyHealth #GeneTherapy120Share
David Hernandez+FollowGene Therapy Drama: 2nd Elevidys DeathBig news in the gene therapy world: another patient has died after getting Sarepta’s Elevidys for Duchenne muscular dystrophy, again due to acute liver failure—a known risk with these treatments. Sarepta’s now pausing shipments for non-ambulatory patients and putting new safety steps in place, including possibly adding another immunosuppressant. Investors are spooked, and there’s talk about whether Elevidys could get pulled for some patients. The whole gene therapy field is feeling the heat right now! #GeneTherapy #Elevidys #DMD #Health #BodyHealth40Share
Jacqueline Howard DDS+FollowGene Therapy Drama: 2nd Death Shakes SareptaSarepta’s gene therapy for muscular dystrophy just hit another major snag—a second teen has died from liver injury after treatment. The company’s now pausing shipments for older, non-walking patients and rethinking safety protocols. The FDA might step in and tighten the rules or even pull the drug for some patients. Wild part? This one-time treatment costs $3.2 million. Wall Street’s freaking out, and Sarepta’s stock just tanked 42%. Stay tuned for more twists. #GeneTherapy #MuscularDystrophy #BiotechNews #Health #BodyHealth50Share
rachel60+FollowBaby’s Life Saved by Custom Gene TherapyA baby born with a super rare, deadly disorder just became the first person ever to get a one-of-a-kind, personalized gene therapy—and it’s working! KJ Muldoon was facing a future of strict diets, risky transplants, and scary odds, but thanks to a CRISPR-based treatment made just for him, he’s now thriving and hitting milestones. Even when he got sick (which usually means disaster for kids like him), he bounced back like a champ. This could totally change the game for rare diseases! #GeneTherapy #MedicalBreakthrough #CRISPR #RareDisease #ScienceNews #Health190Share
Kristi Key+FollowGene Therapy Breakthrough for ThalassemiaDid you know gene therapy is actually changing lives for people with beta-thalassemia? Docs at CHOP just shared real-world results with beti-cel (Zynteglo), and patients are finally ditching those constant blood transfusions. The catch? Some need more platelet support, but overall, it’s a game-changer. Experts say these new therapies are not just effective—they’re curative for thalassemia and even sickle cell. Feels like we’re witnessing a medical revolution! #GeneTherapy #Thalassemia #MedicalBreakthrough #Healthcare #BloodDisorders #Health00Share
jporter+FollowCardiology’s April Plot Twists RevealedApril was wild for heart health news! VERVE-102 gene therapy got FDA Fast Track status after slashing LDL-C by up to 70% in early trials—major hope for high cholesterol. Meanwhile, mavacamten stumbled in a big trial for non-obstructive HCM, but the FDA made it easier to use for obstructive HCM. Plus, combo cholesterol meds are saving more lives post-heart attack, and a new pacemaker tech just got Breakthrough Device status. Cardiology is seriously leveling up! #Cardiology #GeneTherapy #FDAnews #HeartHealth #MedicalInnovation #Health120Share
james60+Follow5 Wild Healthcare Updates in 5 MinutesDid you catch these game-changing healthcare headlines? 1) The FDA just approved pz-cel, the first-ever gene therapy for RDEB—huge for wound healing! 2) Upadacitinib got the green light for giant cell arteritis, meaning less steroid drama. 3) Nipocalimab is now an option for teens with gMG. 4) Semaglutide’s latest trial shows it can seriously help with liver disease. 5) And heads up: high blood sugar in teens could mean heart trouble later, especially for girls. Wild week! #HealthcareNews #FDA #GeneTherapy #MedicalBreakthroughs #HealthUpdate #Health100Share
Keith Stokes+Follow5 Wild Healthcare Breakthroughs This WeekDid you see the FDA just approved the first-ever gene therapy for a rare skin disorder? Plus, there’s a new treatment for giant cell arteritis that could help patients ditch steroids. Myasthenia gravis got a new med, semaglutide is showing promise for MASH, and a global study found high teen blood sugar could mean bigger heart risks later. Healthcare is moving FAST—these headlines are game-changers! #HealthcareNews #FDAApprovals #MedicalBreakthroughs #GeneTherapy #Pharma #Health391Share
Joseph Bradley+FollowGene Therapy Gave This Kid a Second ChanceImagine being told your child has a 'death sentence' disease—and then watching him go from hospital beds to playing football at school. That’s Eisa’s story. Born with a rare immune disorder (LAD-1), he had no donor match for a transplant. But a groundbreaking gene therapy trial changed everything. Now, Eisa’s living a normal, happy life, and this treatment could be a game-changer for other rare diseases. Science is wild, right? #GeneTherapy #MedicalBreakthrough #FeelGoodNews #ScienceWin #Health6843Share
vnguyen+FollowCan AI Crack Alzheimer’s Code?AI just helped scientists uncover a hidden gene function behind Alzheimer’s, and now there’s a new molecule, NCT-503, showing promise in mouse models. Imagine targeting the disease at its genetic roots, not just treating symptoms. But how close are we to a real breakthrough, and what hurdles remain before this hits human trials? Would you trust an AI-discovered drug for brain health? Let’s debate the future of neurotech! #AlzheimersResearch #AIDiscovery #Neurotech #GeneTherapy #FutureOfMedicine #Tech100Share
